Sarepta Reports Second Death of Patient Using Its Gene Therapy

 

Sarepta Therapeutics Inc. said a second patient has died of acute liver failure after being treated with its gene therapy for a rare muscle disorder.

The death comes three months after a teenage boy died after getting the one-time treatment, Elevidys. Both cases occurred in patients with Duchenne muscular dystrophy who are unable to walk, the company said.

https://www.bloomberg.com/news/articles/2025-06-15/sarepta-reports-second-death-of-patient-using-its-gene-therapy