Bluebird (NASDAQ:BLUE) comments on long-term safety and efficacy data for LentiGlobin gene therapy for Transfusion-dependent β-Thalassemia.
In the Phase 1/2 Northstar study, patients with TDT who don’t have a β0/β0 genotype achieved up to 3.8 years of transfusion independence.
In the ongoing Phase 3 Northstar-2 study, four of five evaluable study patients (with TDT, without β0/β0 genotype) achieved transfusion independence.
No comments:
Post a Comment
Note: Only a member of this blog may post a comment.