Jaguar Gets Euro Orphan Drug Tag for Second Rare Disease Indication

 MVID, a rare congenital diarrheal disorder (CDD) condition, is a life-threatening autosomal recessive disease that affects newborns and children and leads to significant morbidity and mortality from intestinal failure, including severe secretory diarrhea

Presentation expected in December 2022 of initial results of an investigator-initiated proof-of-concept trial of crofelemer for CDD and short bowel syndrome (SBS) with intestinal failure, supporting the potential for expanded patient access to crofelemer in 2023 in Europe

https://finance.yahoo.com/news/european-medicines-agency-grants-orphan-123000861.html