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Tuesday, April 18, 2023

Precision to Present Duchenne Research at American Society of Gene & Cell Therapy

 Presentation to Highlight Preclinical Development Progress of PBGENE-DMD Program for Potential Treatment of Duchenne Muscular Dystrophy

Precision BioSciences, Inc. (Nasdaq: DTIL), a clinical stage gene editing company developing ARCUS®-based ex vivo allogeneic CAR T and in vivo gene editing therapies, today announced that a late-breaking abstract featuring preclinical data from its PBGENE-DMD program for the potential treatment of Duchenne muscular dystrophy (DMD), was selected for an oral presentation at the American Society of Gene & Cell Therapy (ASGCT) 26th Annual Meeting being held May 16-20, 2023 in Los Angeles, CA.

"ARCUS nucleases have been shown to be exceptionally versatile for complex gene editing approaches, including large gene excisions. The goal of the PBGENE-DMD program is to utilize a pair of ARCUS nucleases, delivered by a single AAV, that are designed to excise an approximately 500,000 base pair mutation "hot spot" region from the dystrophin gene in order to make a variant of the dystrophin protein that is functionally competent," said Jeff Smith, Chief Research Officer of Precision BioSciences. "We look forward to the upcoming ASGCT presentation highlighting new data from Precision’s DMD gene editing program."

The abstract will be publicly accessible through the ASGCT website at https://annualmeeting.asgct.org/abstracts beginning on May 2, 2023.

https://finance.yahoo.com/news/precision-biosciences-announces-breaking-abstract-120000107.html

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