Search This Blog

Monday, September 28, 2020

Sarepta up on positive gene therapy data in muscular dystrophy

Sarepta Therapeutics (NASDAQ:SRPT) perks up 2% premarket on light volume on the heels of updated follow-up data on two of its gene therapy candidates.

SRP-9003 in limb-girdle muscular dystrophy: 18-month functional data from three subjects in the low-dose cohort and six-month functional data from three participants in the high-dose arm showed improvements from baseline across all functional measures. No new treatment-related safety signals have been observed.

SRP-9001 in Duchenne muscular dystrophy (DMD): Two-year follow-up results from four patients showed a mean increase of 7.0 points (5.5 points at year one) from baseline in a scale measuring functional motor abilities in ambulatory DMD patients called NSAA (scale range is 0-34).

Development is ongoing.

https://seekingalpha.com/news/3617642-sarapta-up-2-on-positive-gene-therapy-data-in-muscular-dystrophy

No comments:

Post a Comment

Note: Only a member of this blog may post a comment.