Search This Blog

Monday, March 2, 2026

uniQure says FDA finds AMT-130 Phase I/II data insufficient

 

 as 2025 results show loss and cash runway to 2H 2029

  • FDA deemed AMT-130 Phase I/II data versus an external control insufficient to support a marketing application.
  • Agency recommended a new randomized sham surgery-controlled trial, and uniQure plans further talks on Phase III design.
  • uniQure ended 2025 with $622.5 million in cash, expected to fund operations into the second half of 2029.
  • 2025 revenue totaled $16.1 million, while the company recorded a $199.0 million net loss for the year.

No comments:

Post a Comment

Note: Only a member of this blog may post a comment.